Advance in therapy for Duchenne/Becker muscular dystrophy / 中国当代儿科杂志
Chinese Journal of Contemporary Pediatrics
; (12): 294-298, 2015.
Article
en Zh
| WPRIM
| ID: wpr-346161
Biblioteca responsable:
WPRO
ABSTRACT
Duchenne/Becker muscular dystrophy (DMD/BMD) is the most common X-linked recessive inherited neuromuscular disease, characterized by progressive muscle weakness. Mutations in the dystrophin gene are responsible for this disease. Treatment for this disease has always been a topic of interest. With the development of diagnosis and treatment technology of molecular biology, promising therapies have been developed. This review article summarizes the advance in traditional therapy, cell transplantation and gene therapy for this disease.
Texto completo:
1
Índice:
WPRIM
Asunto principal:
Terapéutica
/
Terapia Genética
/
Distrofia Muscular de Duchenne
/
Trasplante de Células Madre
/
Usos Terapéuticos
/
Glucocorticoides
Límite:
Humans
Idioma:
Zh
Revista:
Chinese Journal of Contemporary Pediatrics
Año:
2015
Tipo del documento:
Article