Recent research on the treatment of spinal muscular atrophy / 中国当代儿科杂志
Chinese Journal of Contemporary Pediatrics
;
(12): 204-209, 2022.
Artigo
em Inglês
| WPRIM
| ID: wpr-928588
ABSTRACT
Spinal muscular atrophy (SMA) is an autosomal recessive neuromuscular disease characterized by progressive muscular weakness and atrophy. SMA, as an inherited disease, is the leading cause of death in infants and young children. Rapid progress has been made in the research field of SMA in recent years, and some related treatment drugs have been successfully approved for marketing. This article reviews the recent research advances in the treatment of SMA.
Texto completo:
DisponíveL
Índice:
WPRIM (Pacífico Ocidental)
Assunto principal:
Atrofia Muscular Espinal
Limite:
Criança
/
Criança, pré-escolar
/
Humanos
/
Lactente
Idioma:
Inglês
Revista:
Chinese Journal of Contemporary Pediatrics
Ano de publicação:
2022
Tipo de documento:
Artigo
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