1.
Nat Med
; 25(11): 1634-1636, 2019 11.
Article
in English
| MEDLINE
| ID: mdl-31649350
Subject(s)
CRISPR-Cas Systems/genetics , Gene Editing/ethics , Cloning, Organism/ethics , Humans , Infant
2.
Nat Med
; 19(7): 793, 2013 Jul.
Article
in English
| MEDLINE
| ID: mdl-23836201
3.
Nat Med
; 19(2): 121, 2013 Feb.
Article
in English
| MEDLINE
| ID: mdl-23389596
Subject(s)
Factor VIII/administration & dosage , Hemophilia A/drug therapy , Adolescent , Child , Genetic Therapy , Humans , Male
4.
Nat Rev Drug Discov
; 11(11): 819-20, 2012 Nov.
Article
in English
| MEDLINE
| ID: mdl-23123929
5.
Nat Med
; 18(9): 1314, 2012 Sep.
Article
in English
| MEDLINE
| ID: mdl-22961147
6.
Nat Med
; 18(8): 1159, 2012 Aug.
Article
in English
| MEDLINE
| ID: mdl-22869171
Subject(s)
Acetanilides/therapeutic use , Adrenergic beta-Agonists/therapeutic use , Drug Approval/legislation & jurisprudence , Receptors, Adrenergic, beta-3/drug effects , Thiazoles/therapeutic use , Urinary Bladder, Overactive/drug therapy , Humans , United States , United States Food and Drug Administration
7.
Nat Rev Drug Discov
; 11(8): 585-6, 2012 Aug.
Article
in English
| MEDLINE
| ID: mdl-22850771
8.
Nat Rev Drug Discov
; 10(12): 887-8, 2011 Dec 01.
Article
in English
| MEDLINE
| ID: mdl-22129977
9.
Nat Med
; 17(10): 1158, 2011 Oct 11.
Article
in English
| MEDLINE
| ID: mdl-21988964
10.
Nat Rev Drug Discov
; 10(7): 479-80, 2011 Jul 01.
Article
in English
| MEDLINE
| ID: mdl-21720393
Subject(s)
Aminophenols/therapeutic use , Cystic Fibrosis/drug therapy , Cystic Fibrosis/genetics , Drug Discovery , Quinolones/therapeutic use , Clinical Trials as Topic , Cystic Fibrosis/metabolism , Cystic Fibrosis/therapy , Cystic Fibrosis Transmembrane Conductance Regulator/genetics , Cystic Fibrosis Transmembrane Conductance Regulator/metabolism , Drug Approval , Humans , Mutation
11.
Nat Med
; 17(5): 518, 2011 May.
Article
in English
| MEDLINE
| ID: mdl-21546947
12.
Nat Rev Drug Discov
; 10(5): 323-4, 2011 May.
Article
in English
| MEDLINE
| ID: mdl-21532548
13.
Nat Rev Drug Discov
; 10(2): 81-2, 2011 Feb.
Article
in English
| MEDLINE
| ID: mdl-21283091
14.
Nat Rev Drug Discov
; 9(8): 579-81, 2010 Aug.
Article
in English
| MEDLINE
| ID: mdl-20671750
15.
Nat Rev Drug Discov
; 9(7): 501-3, 2010 Jul.
Article
in English
| MEDLINE
| ID: mdl-20592732
Subject(s)
Antiviral Agents/therapeutic use , Hepatitis C/drug therapy , Oligopeptides/therapeutic use , Clinical Trials, Phase I as Topic , Clinical Trials, Phase III as Topic , Drug Resistance, Viral , Hepacivirus/drug effects , Hepacivirus/genetics , Hepatitis C/virology , Humans , Proline/analogs & derivatives , Proline/therapeutic use , Protease Inhibitors/pharmacology , Protease Inhibitors/therapeutic use
16.
Nat Med
; 16(6): 620, 2010 Jun.
Article
in English
| MEDLINE
| ID: mdl-20526304
17.
Nat Rev Drug Discov
; 9(4): 257-8, 2010 Apr.
Article
in English
| MEDLINE
| ID: mdl-20357793
Subject(s)
Arthritis, Rheumatoid/drug therapy , Drug Delivery Systems , Protein Kinase Inhibitors/pharmacology , Administration, Oral , Aminopyridines , Arthritis, Rheumatoid/physiopathology , Clinical Trials as Topic , Drug Design , Humans , Morpholines , Oxazines/pharmacology , Oxazines/therapeutic use , Piperidines , Protein Kinase Inhibitors/therapeutic use , Pyridines/pharmacology , Pyridines/therapeutic use , Pyrimidines/pharmacology , Pyrimidines/therapeutic use , Pyrroles/pharmacology , Pyrroles/therapeutic use
18.
Nat Med
; 16(2): 140, 2010 Feb.
Article
in English
| MEDLINE
| ID: mdl-20134449
19.
Nat Rev Drug Discov
; 8(10): 757-8, 2009 Oct.
Article
in English
| MEDLINE
| ID: mdl-19794432
Subject(s)
Bone Density Conservation Agents/administration & dosage , Osteoporosis/drug therapy , Antibodies, Monoclonal/administration & dosage , Antibodies, Monoclonal, Humanized , Bone Density/drug effects , Bone Density/physiology , Denosumab , Drug Delivery Systems/methods , Drug Delivery Systems/trends , Humans , Osteoporosis/pathology , RANK Ligand/administration & dosage , Time Factors
20.
Nat Med
; 15(8): 831, 2009 Aug.
Article
in English
| MEDLINE
| ID: mdl-19661979