1.
Rev Neurol (Paris)
; 170(12): 799-807, 2014 Dec.
Artículo
en Inglés
| MEDLINE
| ID: mdl-25459122
RESUMEN
This review focuses on the most recent data on biotherapeutic approaches, using DNA, RNA, recombinant proteins, or cells as therapeutic tools or targets for the treatment of neuromuscular diseases. Many of these novel technologies have now reached the clinical stage and have or are about to move to the market. Others, like genome editing are still in an early stage but hold great promise.