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Longitudinal quality of life analysis in a phenylketonuria cohort provided sapropterin dihydrochloride.
Douglas, Teresa D; Ramakrishnan, Usha; Kable, Julie A; Singh, Rani H.
Affiliation
  • Singh RH; Metabolic Nutrition Program, Division of Medical Genetics, Emory Department of Human Genetics, 2165 North Decatur Road, Decatur, GA 30033, USA. rsingh@emory.edu.
Health Qual Life Outcomes ; 11: 218, 2013 Dec 30.
Article in En | MEDLINE | ID: mdl-24373161

Full text: 1 Collection: 01-internacional Database: MEDLINE Main subject: Phenylketonurias / Quality of Life / Biopterins Type of study: Observational_studies / Qualitative_research / Risk_factors_studies Aspects: Patient_preference Limits: Adolescent / Adult / Child / Female / Humans / Male / Middle aged Country/Region as subject: America do norte Language: En Journal: Health Qual Life Outcomes Journal subject: SAUDE PUBLICA Year: 2013 Document type: Article Country of publication: United kingdom

Full text: 1 Collection: 01-internacional Database: MEDLINE Main subject: Phenylketonurias / Quality of Life / Biopterins Type of study: Observational_studies / Qualitative_research / Risk_factors_studies Aspects: Patient_preference Limits: Adolescent / Adult / Child / Female / Humans / Male / Middle aged Country/Region as subject: America do norte Language: En Journal: Health Qual Life Outcomes Journal subject: SAUDE PUBLICA Year: 2013 Document type: Article Country of publication: United kingdom