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Utility of Self-Destructing CRISPR/Cas Constructs for Targeted Gene Editing in the Retina.
Li, Fan; Hung, Sandy S C; Mohd Khalid, Mohd Khairul Nizam; Wang, Jiang-Hui; Chrysostomou, Vicki; Wong, Vickie H Y; Singh, Vikrant; Wing, Kristof; Tu, Leilei; Bender, James A; Pébay, Alice; King, Anna E; Cook, Anthony L; Wong, Raymond C B; Bui, Bang V; Hewitt, Alex W; Liu, Guei-Sheung.
Afiliación
  • Li F; Menzies Institute for Medical Research, University of Tasmania, Hobart, Australia.
  • Hung SSC; Centre for Eye Research Australia, Royal Victorian Eye and Ear Hospital, East Melbourne, Australia.
  • Mohd Khalid MKN; State Key Laboratory of Ophthalmology, Zhongshan Ophthalmic Centre, Sun Yat-sen University, Guangzhou, China.
  • Wang JH; Centre for Eye Research Australia, Royal Victorian Eye and Ear Hospital, East Melbourne, Australia.
  • Chrysostomou V; Menzies Institute for Medical Research, University of Tasmania, Hobart, Australia.
  • Wong VHY; Centre for Eye Research Australia, Royal Victorian Eye and Ear Hospital, East Melbourne, Australia.
  • Singh V; Ophthalmology, Department of Surgery, University of Melbourne, East Melbourne, Australia.
  • Wing K; Centre for Eye Research Australia, Royal Victorian Eye and Ear Hospital, East Melbourne, Australia.
  • Tu L; Ophthalmology, Department of Surgery, University of Melbourne, East Melbourne, Australia.
  • Bender JA; Department of Optometry and Vision Sciences, University of Melbourne, Parkville, Australia.
  • Pébay A; Menzies Institute for Medical Research, University of Tasmania, Hobart, Australia.
  • King AE; Menzies Institute for Medical Research, University of Tasmania, Hobart, Australia.
  • Cook AL; Department of Ophthalmology, Jinan University, Guangzhou, China.
  • Wong RCB; Wicking Dementia Research and Education Centre, University of Tasmania, Hobart, Australia.
  • Bui BV; Centre for Eye Research Australia, Royal Victorian Eye and Ear Hospital, East Melbourne, Australia.
  • Hewitt AW; Ophthalmology, Department of Surgery, University of Melbourne, East Melbourne, Australia.
  • Liu GS; Department of Anatomy and Neuroscience, University of Melbourne, Parkville, Australia.
Hum Gene Ther ; 30(11): 1349-1360, 2019 11.
Article en En | MEDLINE | ID: mdl-31373227

Texto completo: 1 Colección: 01-internacional Base de datos: MEDLINE Asunto principal: Retina / Sistemas CRISPR-Cas / Edición Génica Límite: Animals / Humans Idioma: En Revista: Hum Gene Ther Asunto de la revista: GENETICA MEDICA / TERAPEUTICA Año: 2019 Tipo del documento: Article País de afiliación: Australia Pais de publicación: Estados Unidos

Texto completo: 1 Colección: 01-internacional Base de datos: MEDLINE Asunto principal: Retina / Sistemas CRISPR-Cas / Edición Génica Límite: Animals / Humans Idioma: En Revista: Hum Gene Ther Asunto de la revista: GENETICA MEDICA / TERAPEUTICA Año: 2019 Tipo del documento: Article País de afiliación: Australia Pais de publicación: Estados Unidos