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Short-term treatment of golden retriever muscular dystrophy (GRMD) dogs with rAAVrh74.MHCK7.GALGT2 induces muscle glycosylation and utrophin expression but has no significant effect on muscle strength.
Martin, Paul T; Zygmunt, Deborah A; Ashbrook, Anna; Hamilton, Sonia; Packer, Davin; Birch, Sharla M; Bettis, Amanda K; Balog-Alvarez, Cynthia J; Guo, Lee-Jae; Nghiem, Peter P; Kornegay, Joe N.
Afiliación
  • Martin PT; Center for Gene Therapy, Abigail Wexner Research Institute, Nationwide Children's Hospital, Columbus, Ohio, United States of America.
  • Zygmunt DA; Department of Pediatrics, The Ohio State University College of Medicine, Columbus, Ohio, United States of America.
  • Ashbrook A; Center for Gene Therapy, Abigail Wexner Research Institute, Nationwide Children's Hospital, Columbus, Ohio, United States of America.
  • Hamilton S; Center for Gene Therapy, Abigail Wexner Research Institute, Nationwide Children's Hospital, Columbus, Ohio, United States of America.
  • Packer D; Neuroscience Undergraduate Program, The Ohio State University, Columbus, Ohio, United States of America.
  • Birch SM; Neuroscience Graduate Program, The Ohio State University, Columbus, Ohio, United States of America.
  • Bettis AK; Department of Veterinary Integrative Biosciences, College of Veterinary Medicine and Biomedical Sciences, Texas A&M University, College Station, TX, United States of America.
  • Balog-Alvarez CJ; Department of Veterinary Integrative Biosciences, College of Veterinary Medicine and Biomedical Sciences, Texas A&M University, College Station, TX, United States of America.
  • Guo LJ; Department of Veterinary Integrative Biosciences, College of Veterinary Medicine and Biomedical Sciences, Texas A&M University, College Station, TX, United States of America.
  • Nghiem PP; Department of Veterinary Integrative Biosciences, College of Veterinary Medicine and Biomedical Sciences, Texas A&M University, College Station, TX, United States of America.
  • Kornegay JN; Department of Veterinary Integrative Biosciences, College of Veterinary Medicine and Biomedical Sciences, Texas A&M University, College Station, TX, United States of America.
PLoS One ; 16(3): e0248721, 2021.
Article en En | MEDLINE | ID: mdl-33770101

Texto completo: 1 Colección: 01-internacional Base de datos: MEDLINE Asunto principal: Terapia Genética / Distrofina / Glicosiltransferasas / Distrofia Muscular de Duchenne / Enfermedades de los Perros / Distrofias Musculares Límite: Animals / Humans Idioma: En Revista: PLoS One Asunto de la revista: CIENCIA / MEDICINA Año: 2021 Tipo del documento: Article País de afiliación: Estados Unidos

Texto completo: 1 Colección: 01-internacional Base de datos: MEDLINE Asunto principal: Terapia Genética / Distrofina / Glicosiltransferasas / Distrofia Muscular de Duchenne / Enfermedades de los Perros / Distrofias Musculares Límite: Animals / Humans Idioma: En Revista: PLoS One Asunto de la revista: CIENCIA / MEDICINA Año: 2021 Tipo del documento: Article País de afiliación: Estados Unidos