Your browser doesn't support javascript.
loading
Investigating the Impact of Delivery Routes for Exon Skipping Therapies in the CNS of DMD Mouse Models.
Saoudi, Amel; Fergus, Claire; Gileadi, Talia; Montanaro, Federica; Morgan, Jennifer E; Kelly, Vincent P; Tensorer, Thomas; Garcia, Luis; Vaillend, Cyrille; Muntoni, Francesco; Goyenvalle, Aurélie.
Afiliación
  • Saoudi A; Université Paris-Saclay, UVSQ, Inserm, END-ICAP, 78000 Versailles, France.
  • Fergus C; Université Paris-Saclay, CNRS, Institut des Neurosciences Paris-Saclay, 91400 Saclay, France.
  • Gileadi T; School of Biochemistry & Immunology, Trinity Biomedical Sciences Institute, Trinity College Dublin, D02 R590 Dublin, Ireland.
  • Montanaro F; Dubowitz Neuromuscular Centre, UCL Great Ormond Street Institute of Child Health, 30 Guildford Street, London WC1N 1EH, UK.
  • Morgan JE; Dubowitz Neuromuscular Centre, UCL Great Ormond Street Institute of Child Health, 30 Guildford Street, London WC1N 1EH, UK.
  • Kelly VP; Dubowitz Neuromuscular Centre, UCL Great Ormond Street Institute of Child Health, 30 Guildford Street, London WC1N 1EH, UK.
  • Tensorer T; School of Biochemistry & Immunology, Trinity Biomedical Sciences Institute, Trinity College Dublin, D02 R590 Dublin, Ireland.
  • Garcia L; SQY Therapeutics-Synthena, UVSQ, 78180 Montigny le Bretonneux, France.
  • Vaillend C; Université Paris-Saclay, UVSQ, Inserm, END-ICAP, 78000 Versailles, France.
  • Muntoni F; Université Paris-Saclay, CNRS, Institut des Neurosciences Paris-Saclay, 91400 Saclay, France.
  • Goyenvalle A; Dubowitz Neuromuscular Centre, UCL Great Ormond Street Institute of Child Health, 30 Guildford Street, London WC1N 1EH, UK.
Cells ; 12(6)2023 03 15.
Article en En | MEDLINE | ID: mdl-36980249

Texto completo: 1 Colección: 01-internacional Base de datos: MEDLINE Asunto principal: Distrofina / Distrofia Muscular de Duchenne Tipo de estudio: Prognostic_studies Límite: Animals Idioma: En Revista: Cells Año: 2023 Tipo del documento: Article País de afiliación: Francia

Texto completo: 1 Colección: 01-internacional Base de datos: MEDLINE Asunto principal: Distrofina / Distrofia Muscular de Duchenne Tipo de estudio: Prognostic_studies Límite: Animals Idioma: En Revista: Cells Año: 2023 Tipo del documento: Article País de afiliación: Francia