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Interim analysis: Open-label extension study of leniolisib for patients with APDS.
Rao, V Koneti; Kulm, Elaine; Sedivá, Anna; Plebani, Alessandro; Schuetz, Catharina; Shcherbina, Anna; Dalm, Virgil A; Trizzino, Antonino; Zharankova, Yulia; Webster, Sharon; Orpia, Alanvin; Körholz, Julia; Lougaris, Vassilios; Rodina, Yulia; Radford, Kath; Bradt, Jason; Relan, Anurag; Holland, Steven M; Lenardo, Michael J; Uzel, Gulbu.
Afiliación
  • Rao VK; National Institute of Allergy and Infectious Diseases, National Institutes of Health, Bethesda, Md. Electronic address: korao@niaid.nih.gov.
  • Kulm E; Clinical Research Directorate, Frederick National Laboratory for Cancer Research, Bethesda, Md.
  • Sedivá A; Department of Immunology, 2nd Faculty of Medicine, Charles University and Motol University Hospital, Prague, Czech Republic.
  • Plebani A; Pediatrics Clinic, Department of Clinical and Experimental Sciences, University of Brescia, ASST Spedali Civili of Brescia, Brescia, Italy.
  • Schuetz C; Department of Pediatric Immunology, University Hospital Carl Gustav Carus, Technische Universität Dresden, Dresden, Germany.
  • Shcherbina A; Department of Immunology, Dmitry Rogachev National Medical Research Center of Pediatric Hematology, Oncology and Immunology, Moscow, Russia.
  • Dalm VA; Division of Allergy & Clinical Immunology, Department of Internal Medicine, Rotterdam, The Netherlands; Department of Immunology, Erasmus MC University Medical Center, Rotterdam, The Netherlands.
  • Trizzino A; Department of Pediatric Hematology and Oncology, ARNAS Civico Di Cristina Benfratelli Hospital, Palermo, Italy.
  • Zharankova Y; Belarusian Research Center for Pediatric Oncology, Hematology and Immunology, Minsk, Belarus.
  • Webster S; National Institute of Allergy and Infectious Diseases, National Institutes of Health, Bethesda, Md.
  • Orpia A; National Institute of Allergy and Infectious Diseases, National Institutes of Health, Bethesda, Md.
  • Körholz J; Department of Pediatric Immunology, University Hospital Carl Gustav Carus, Technische Universität Dresden, Dresden, Germany.
  • Lougaris V; Pediatrics Clinic, Department of Clinical and Experimental Sciences, University of Brescia, ASST Spedali Civili of Brescia, Brescia, Italy.
  • Rodina Y; Department of Immunology, Dmitry Rogachev National Medical Research Center of Pediatric Hematology, Oncology and Immunology, Moscow, Russia.
  • Radford K; Novartis Pharmaceuticals UK Ltd, London, United Kingdom.
  • Bradt J; Pharming Healthcare, Inc, Warren, NJ.
  • Relan A; Pharming Healthcare, Inc, Warren, NJ.
  • Holland SM; National Institute of Allergy and Infectious Diseases, National Institutes of Health, Bethesda, Md.
  • Lenardo MJ; National Institute of Allergy and Infectious Diseases, National Institutes of Health, Bethesda, Md.
  • Uzel G; National Institute of Allergy and Infectious Diseases, National Institutes of Health, Bethesda, Md.
J Allergy Clin Immunol ; 153(1): 265-274.e9, 2024 01.
Article en En | MEDLINE | ID: mdl-37797893

Texto completo: 1 Colección: 01-internacional Base de datos: MEDLINE Asunto principal: Linfadenopatía / Síndromes de Inmunodeficiencia Tipo de estudio: Clinical_trials Aspecto: Patient_preference Límite: Adult / Female / Humans / Male Idioma: En Revista: J Allergy Clin Immunol Año: 2024 Tipo del documento: Article

Texto completo: 1 Colección: 01-internacional Base de datos: MEDLINE Asunto principal: Linfadenopatía / Síndromes de Inmunodeficiencia Tipo de estudio: Clinical_trials Aspecto: Patient_preference Límite: Adult / Female / Humans / Male Idioma: En Revista: J Allergy Clin Immunol Año: 2024 Tipo del documento: Article