Advance in therapy for Duchenne/Becker muscular dystrophy / 中国当代儿科杂志
Chinese Journal of Contemporary Pediatrics
; (12): 294-298, 2015.
Artigo
em Chinês
| WPRIM (Pacífico Ocidental)
| ID: wpr-346161
Biblioteca responsável:
WPRO
ABSTRACT
Duchenne/Becker muscular dystrophy (DMD/BMD) is the most common X-linked recessive inherited neuromuscular disease, characterized by progressive muscle weakness. Mutations in the dystrophin gene are responsible for this disease. Treatment for this disease has always been a topic of interest. With the development of diagnosis and treatment technology of molecular biology, promising therapies have been developed. This review article summarizes the advance in traditional therapy, cell transplantation and gene therapy for this disease.
Texto completo:
Disponível
Base de dados:
WPRIM (Pacífico Ocidental)
Assunto principal:
Terapêutica
/
Terapia Genética
/
Distrofia Muscular de Duchenne
/
Transplante de Células-Tronco
/
Usos Terapêuticos
/
Glucocorticoides
Limite:
Humanos
Idioma:
Chinês
Revista:
Chinese Journal of Contemporary Pediatrics
Ano de publicação:
2015
Tipo de documento:
Artigo